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Results for search "Gene Therapy".

Health News Results - 27

MONDAY, June 3, 2019 (HealthDay News) -- Last year, a scientist from China created a storm of controversy when he claimed he'd used gene-editing technology to create "designer" twin babies. Now, a new study is highlighting one of the dangers of that endeavor.

Researchers have found that the gene mutation the scientist used -- affecting a gene called CCR5 -- is associated with a shorte...

WEDNESDAY, May 1, 2019 (HealthDay News) -- A gene therapy that tweaks the immune system might offer hope to people with blood cancer that has resisted standard treatments, a new preliminary trial suggests.

The cancer, called multiple myeloma, arises in certain white blood cells. It is currently incurable, but there are treatments that can help people live w...

WEDNESDAY, April 17, 2019 (HealthDay News) -- They were once imprisoned in plastic bubbles that cut them off from the dangerous, infectious world.

But now, children born with a disease that robs them of a functioning immune system may have gained a new lease on life.

Researchers say gene therapy may be a cure for X-linked severe combined immune deficiency (SCID-X1), widely ...

WEDNESDAY, March 13, 2019 (HealthDay News) -- The controversy over a Chinese scientist who claimed he created gene-edited babies has prompted the U.S. National Institutes of Health to join an international moratorium on such research.

"Today, leading scientists and ethicists from seven countries have called for an international moratorium on the use of genetic editing to modify the hu...

MONDAY, Jan. 28, 2019 (HealthDay News) -- The supply of donor organs for infants needing a heart transplant is critically low, but researchers have taken a first step toward using pig hearts to fill the need.

The concept of using animal organs to save human lives has been around for years. With donor organs in short supply, the hope is that animal organs can keep patients alive while ...

FRIDAY, Dec. 14, 2018 (HealthDay News) -- A modified version of the CRISPR gene-editing technique could help fight obesity without having to alter any genes, a new study in mice suggests.

CRISPR, an acronym for a family of DNA sequences, generally involves cutting or editing DNA to correct genetic defects that cause disease.

This new technique boosts the activity of certain ge...

TUESDAY, Dec. 4, 2018 (HealthDay News) -- A new gene therapy shows early promise against sickle cell anemia, researchers say.

The therapy targets the genetic flaw that causes sickle cell. In a small group of patients, researchers said the therapy appears safe and effective enough to keep moving forward into larger trials.

"We've been talking about using gene therapy for sick...

WEDNESDAY, Nov. 28, 2018 (HealthDay News) -- An experimental gene therapy for Parkinson's disease seems to work by rewiring key areas of the brain, a new study finds.

The researchers focused on 15 Parkinson's patients who, in an earlier trial, had received so-called GAD gene therapy. GAD is an enzyme that spurs the production of a brain chemical involved in movement control.

THURSDAY, Oct. 25, 2018 (HealthDay News) -- A new gene therapy might help improve motor symptoms in people with Parkinson's disease who aren't responding to other therapies, an early study has found.

"This is not a cure of Parkinson's disease," said James Beck, chief scientific officer of the Parkinson's Foundation. "This is a potentially good treatment for symptom control. It provid...

THURSDAY, Aug. 30, 2018 (HealthDay News) -- For the first time, scientists report using gene-editing technology to halt the progression of muscular dystrophy in dogs -- suggesting a possible breakthrough for children with a form of the disease.

Reporting in the current issue of Science, researchers describe how they used CRISPR technology to edit a naturally occurring genetic f...

FRIDAY, July 27, 2018 (HealthDay News) -- Gene editing is no longer just fodder for sci-fi movies. Most Americans believe it's OK to tweak a baby's DNA under certain circumstances, a new poll finds.

The Pew Research Center, based in Washington, D.C., found almost three-quarters of Americans approve of gene editing to prevent serious health problems in babies.

But tampering ...

MONDAY, July 23, 2018 (HealthDay News) -- It's only worked in mice so far, but scientists report a finding that might pave a path to erase the signs of aging in humans.

In the new study, the researchers focused on the function of mitochondria, the powerhouses of cells. They produce 90 percent of the chemical energy that cells need to survive, according to the study.

When the...

WEDNESDAY, April 25, 2018 (HealthDay News) -- Doctors say they've found a way to head off a rare birth defect that causes babies to be born without functioning sweat glands.

By introducing a specific protein into the womb, researchers prevented the defect from taking hold in three children.

This is the first and only therapy shown to prevent the birth defect, said lead resea...

WEDNESDAY, April 18, 2018 (HealthDay News) -- Wanda Sihanath didn't like the fact that her inherited blood disorder would not allow her to travel far from Chicago to attend college, but what could she do?

Without regular transfusions and blood testing, the beta-thalassemia she inherited from her parents could eventually cause her to become dangerously anemic.

"I wasn't happy...

FRIDAY, April 6, 2018 (HealthDay News) -- Imagine a world in black and white.

That's the plight of people with an extremely rare condition called blue cone monochromacy, an inherited eye disease that renders people unable to see color.

But there's a glimmer of hope for the one in every 100,000 people with the condition: Scientists report that gene therapy improved color visi...

WEDNESDAY, Jan. 3, 2018 (HealthDay News) -- Gene therapy may have the potential to eradicate HIV in people infected with the virus, new animal research suggests.

The science centers around the use of "chimeric antigen receptor" (CAR) genes. In laboratory work with monkeys, these engineered cells have destroyed HIV-infected cells for more than two years, scientists reported.

THURSDAY, Dec. 28, 2017 (HealthDay News) -- The millions of Americans caught in the grip of an addiction to opioids -- prescription painkillers or heroin -- remained the leading health news story of the past year.

The scourge is now so widespread that, just last week, research suggested that deaths from opioid overdoses may be the biggest factor driving a d...

TUESDAY, Dec. 19, 2017 (HealthDay News) -- A new gene therapy to treat children and adults with a rare type of inherited vision loss has been approved by the U.S. Food and Drug Administration.

It's the first gene therapy approved in the United States for a disease caused by mutations in a specific gene, and only the third gene therapy ever approved.

People with this disorder...

SATURDAY, Dec. 9, 2017 (HealthDay News) -- Babies born with the immune-system ravaging "bubble boy" disease have had to spend their too-often-short lives in germ-free isolation, lest something as simple as a common cold virus fell them with a fatal infection.

But after decades of research, doctors now believe they have created a cure for severe combined imm...

SATURDAY, Dec. 9, 2017 (HealthDay News) -- Coming just days after reports of a gene therapy that pushed the bleeding disorder hemophilia B into remission, new research suggests the same could be true for adults with the "A" form of the disease.

That's significant because, due to the complexities of the gene responsible for hemophilia A, experts had thought ...

WEDNESDAY, Dec. 6, 2017 (HealthDay News) -- Gene therapy has helped 10 men with a form of the bleeding disorder hemophilia produce a critical blood clotting factor. This could eliminate the need for tedious and costly standard treatments, researchers report.

While saying the one-time gene therapy was an ideal treatment goal because of its effects, the researchers stopped short of cal...

WEDNESDAY, Nov. 1, 2017 (HealthDay News) -- Babies born with a previously untreatable degenerative nerve disease now have two fresh sources of hope for their future.

Two innovative new therapies for spinal muscular atrophy (SMA) type 1 have proven highly effective in clinical trials, researchers report.

Babies with SMA are born without the gene that promotes production of su...

FRIDAY, Oct. 27, 2017 (HealthDay News) -- A new form of gene therapy shows promise in battling recurrent brain cancer.

The phase 1 clinical trial included 56 patients with recurrent high-grade glioma brain cancer.

Three years after the gene therapy treatment, more than a quarter of the patients were still alive. Median survival for patients was 14.4 months, compared with eig...

THURSDAY, Sept. 28, 2017 (HealthDay News) -- Two new methods of genetic modification may reduce the risk of mosquitoes spreading the infectious disease malaria to people, researchers report.

Malaria kills more than 400,000 people worldwide each year. It's a disease that's transmitted by mosquitoes to people. The majority of those who die from the disease are children aged 5 and under ...

WEDNESDAY, Aug. 30, 2017 (HealthDay News) -- The U.S. Food and Drug Administration broke new ground in cancer care Wednesday by approving the first gene therapy for patients in the United States.

Kymriah (tisagenlecleucel) genetically tweaks a patient's own immune system cells into what scientists call "a living drug" to battle a form of acute lymphoblastic leukemia (ALL).

T...

THURSDAY, Aug. 3, 2017 (HealthDay News) -- Scientists have created genetically altered skin cells that may control type 2 diabetes in lab mice. And they believe the general concept could someday be used to treat various diseases.

Using a combination of stem cells and "gene editing," the researchers created patches of skin cells that were able to release a hormone called GLP1 in a cont...

WEDNESDAY, Aug. 2, 2017 (HealthDay News) -- In a first-ever experiment, geneticists have successfully modified a human embryo to remove a mutation that causes a life-threatening heart condition.

This is the first study to demonstrate that a gene-editing technique can be used in human embryos to convert mutant genes back to their normal version, the researchers said.

The new...